Search Results
The GM1 Gangliosidosis Externally-Led Patient-Focused Drug Development Meeting (EL-PFDD)
GM2 Externally-Led Patient-Focused Drug Development Meeting (EL-PFDD)
Cure Kinley and Kennedy - GM1 EL-PFDD
A Story of Hope and Fight for Life, Nella's Fight, Juvenile GM1 Gangliosidosis, GM1 EL-PFDD
Pancreatitis Externally-Led Patient-Focused Drug Development Meeting (Full Program)
Baby Dean's Story with Type 1 Infantile GM1 Gangliosidosis, GM1 EL-PFDD
Externally-Led Patient Focused Drug Development (EL-PFDD) Meeting for Phelan-McDermid syndrome (PMS)
Bíborka's Type 1 Infantile GM1 Story - GM1 EL-PFDD
GM1 Gangliosidosis Disease Overview - Dr. Cynthia Tifft
Hypophosphatasia Externally-Led Patient Focused Drug Development Meeting
Hampus, Julia, and Isabella's GM1 Story - GM1 EL-PFDD
Limb-Girdle Muscular Dystrophy Externally-Led Patient-Focused Drug Development (EL-PFDD)
